https://pipelinereview.com/zolgensma-data-shows-rapid-significant-clinically-meaningful-benefit-in-sma-including-prolonged-event-free-survival-motor-milestone-achievement-and-durability-now-up-to-5-years-post-dosing/
Zolgensma® data shows rapid, significant, clinically meaningful benefit in SMA including prolonged event-free survival, motor milestone achievement and durability now up to 5 years post-dosing