https://pipelinereview.com/Idorsia-initiates-MODIFY-a-Phase-3-registration-study-to-assess-lucerastat-as-a-potential-new-treatment-option-for-patients-with-Fabry-disease/
Idorsia initiates MODIFY, a Phase 3 registration study to assess lucerastat as a potential new treatment option for patients with Fabry disease